LITTLE Myles Hughes was born deaf with a dislocated left hip, but it wasn’t until he was two that mum Georgia grew concerned.

The Health Resources and Services Administration is requesting public comments on its recommendation to add metachromatic ...

NFL Star Jim Kelly's Grandbaby Overcomes Health Challenges: His Special Name, Revealed NFL all-star, beloved Buffalo Bills ...

Kendra Riley, founder of Dawning Public Relations, advocates for rare disease screening while growing her successful PR firm in Scottsdale.

Spain has agreed to reimburse Orchard Therapeutics' ex vivo gene therapy for the rare childhood disease metachromatic leukodystrophy.

As she enters the second half of the year, Ahwatukee resident Kendra Riley is find new heights of success for the public ...

The FDA has cleared its first gene therapy for children with metachromatic leukodystrophy (MLD), a rare genetic disorder of the brain and nervous centre. The therapy, Orchard Therapeutics ...

A recent FDA letter to makers and distributors of a decades-old thyroid medication has stoked outrage among a subset of ...

Hall of Famer Jim Kelly reveals his daughter Erin's newborn made a medical breakthrough on the anniversary of his son's death.

Sam Hoskin, alongside sister Vicki and friend Chris Gaffney, will participate in a 24-hour endurance race to support the ...

The Senate nixed a provision to “delink” drug list prices from compensation for PBMs and other drug middlemen days before its ...