September is Peripheral Artery Disease Awareness Month, and knowing the steps to help treat the disease is crucial to living ...

The U.S. Food and Drug Administration has approved Zevra Therapeutics' drug for a rare and fatal genetic disorder, making it ...

Fatty liver disease happens when fat builds up in your liver. This can cause damage, inflammation, and other complications.

Improving sickle cell care by expanding treatment options, advancing new therapies and amplifying the voices of people with ...

Citing the National Policy of Rare Diseases launched by the Ministry of Health and Family Welfare in March 2021, he said that ...

Women had a lower probability of receiving any disease-modifying treatment (DMT) and were even less likely to get ...

The U.S. Food and Drug Administration has approved Elanco Animal Health's skin disease treatment for dogs, the health ...

Rocket Pharmaceuticals announced enrollment completion for phase 2 study using its gene therapy RP-A501 for treatment of male ...

A rare-disease federal incentive program critical to biotech R&D is in jeopardy, writes Leslie Williams, president and CEO of ...

MIPLYFFA is the first FDA-approved treatment for Niemann-Pick disease type C (NPC), an ultra-rare and progressive ...

Aligos Therapeutics said on Thursday its experimental treatment for a serious type of fatty liver disease helped significantly reduce liver fat, meeting the main goal of a mid-stage study.

Scientists have developed new potential therapies that selectively remove aggregated tau proteins, which are associated with Alzheimer's disease, and improve symptoms of neurodegeneration in mice.