美国食品药品管理局 (FDA) 已授予 NS-050/NCNP-03 罕见儿科疾病认定，该药物正在开发用于治疗杜氏肌营养不良症 (Duchenne)。FDA 授予的罕见儿科疾病认定用于治疗影响美国 18 岁以下儿童和不到 200,000 ...

Michelle C. Werner agonized over whether the gene therapy treatment Elevidys was right for her teenage son. But to him, the ...

Japan’s Nippon Shinyaku will acquire European rights for a Duchenne muscular dystrophy disease therapy developed by Capricor ...

美国食品药品管理局 (FDA) 已授予 NS-050/NCNP-03 罕见儿科疾病认定，该药物正在开发用于治疗杜氏肌营养不良症 (Duchenne)。FDA 授予的罕见儿科疾病认定用于治疗影响美国 18 岁以下儿童和不到 200,000 ...

A possible gene therapy approval and a series of major trials readouts set the stage for a busy year of drug development in ...

Jenssen guessed then that two of her daughters, the twins, had a Duchenne mutation, and she knew in her heart that, for at least one of them, that genetic legacy was already developing into disease.

肌营养不良是一种遗传性肌肉变性疾病，主要是由于基因缺陷导致的。 一、儿童型肌营养不良 儿童型肌营养不良一般包括Duchenne型和Becker型两种类型。其中Duchenne型属于最常见的类型，患儿出生后会表现为正常的生长发育情况，在3-5岁左右会出现走路不稳的情况 ...

日前，昆明理工大学灵长类转化医学研究院、省部共建非人灵长类国家重点实验室、昆明理工大学生命科学与技术学院陈永昌、季维智团队，与广州实验室、上海交通大学医学院附属新华医院等机构合作，应用非人灵长类疾病模型解析杜氏肌营养不良症（Duchenne ...

The Neu-REFIX Beta 1,3-1,6 glucan, is an exo-polysaccharide produced by N-163 strain of Aureobasidium Pullulans, available as ...

The Billings Livestock Commission hosted the sixth annual Calves to Cure to help raise money and awareness for Duchenne ...

Cases of atrial arrhythmia in patients with Duchenne muscular dystrophy (DMD) are common but lack a standard solution, and ...

Six-year-old Cooper Wood was diagnosed with Duchenne muscular dystrophy earlier this year. When his parents applied for a one ...